EV
Emma Vardy
@emmavardy2.bsky.social
Physician. Honorary Professor of Geriatric Medicine, University of Manchester. Delirium. Dementia. Quality improvement. Book lover. Mum to daughter with PKU.
1.1k followers662 following1.2k posts
MAJOR news in the Lancet this week in the realm of therapeutics for PKU. #pkuwww.thelancet.com/journals/lan...
Effects of oral sepiapterin on blood Phe concentration in a broad range of patients with phenylketonuria (APHENITY): results of an international, phase 3, randomised, double-blind, placebo-controlled ...
Sepiapterin is a promising oral therapy for individuals with phenylketonuria, was well tolerated, and resulted in significant and clinically meaningful reductions in blood Phe concentration in partici...
EV
Emma Vardy
@emmavardy2.bsky.social
Physician. Honorary Professor of Geriatric Medicine, University of Manchester. Delirium. Dementia. Quality improvement. Book lover. Mum to daughter with PKU.
1.1k followers662 following1.2k posts